Author

Date Item Type No Grouping

Article

Mifepristone alone and in combination with scAAV9-SMN1 gene therapy improves disease phenotypes in Smn2B/- spinal muscular atrophy mice. (2025) Emma R. Sutton, Eve McCallion, Joseph M. Hoolachan, Özge Çetin, Paloma Pacheco-Torres, Saman Rashid, Sihame Bouhmidi, Katie Haynes, Lauren Churchill, Taylor Scaife, Helena Chaytow, Yu-Ting Huang, Stephanie Duguez, Bernard L. Schneider, Thomas H. Gillingwater, Maria Dimitriadi and Melissa Bowerman picture_as_pdf

Autophagy in spinal muscular atrophy: from pathogenic mechanisms to therapeutic approaches. (2024) Saman Rashid and Maria Dimitriadi